Hemophilia B Gene Therapy Breakthrough - NYTimes.com

Links shared publicly online about this topic.

  • 15
    total visits

Hemophilia B Gene Therapy Breakthrough - NYTimes.com

nytimes.com

Hemophilia B is the first well-known disease to appear treatable by gene therapy, a technique with a 20-year record of almost unbroken failure.

View full resource at nytimes.com

Tags:

  • Share

Most Recently Shared on December 11, 2011 at 12:46 am By:

DocSimpson Dr. Terry Simpson

Hemophilia B Gene Therapy Breakthrough: A single injection has helped six patients combat a blood-clotting disea... http://t.co/s5lDT8tU

6 months ago...

FDA grants orphan designation for AMT's hemophilia gene therapy program

news-medical.net — “Amsterdam Molecular Therapeutics, a leader in the field of human gene therapy, announced today that the U.S. Food and Drug Administration has granted orphan drug designation to its gene therapy program for the treatment of hemophilia B.View full resource at news-medical.net

  • View Related
  • Share

Most Recently Shared on January 4, 2012 at 3:35 pm By:

NewsMedical News-Medical.Net Health News

FDA grants orphan designation for AMT's hemophilia gene therapy program: Amsterdam Molecular Therapeutics, a lea... http://t.co/2rQWPl5w

5 months ago...

Landmark Gene Therapy Clinical Trial For Hemophilia B: Commentary And Podcast

medicalnewstoday.com — “A recent article in the New England Journal of Medicine showed that Factor IX gene therapy in patients with hemophilia B was able to convert severe hemophilia to moderate or even mild diseaView full resource at medicalnewstoday.com

  • View Related
  • Share

Most Recently Shared on December 14, 2011 at 11:05 am By:

mnt_blood MNT Blood Health News

Landmark Gene Therapy Clinical Trial For Hemophilia B: Commentary And Podcast http://t.co/Cvdsrvrb #blood #hematology

6 months ago...

Gene therapy achieves early success against hereditary bleeding disorder

stjude.org — “Gene therapy achieves early success against hereditary bleeding disorderView full resource at stjude.org

  • View Related
  • Share

Most Recently Shared on December 13, 2011 at 9:21 pm By:

StJude St. Jude Hospital and Children's Hospital

Gene therapy developed by researchers @StJude offers first proof the treatment benefits adults with hemophilia B http://t.co/qDhBUckg

6 months ago...

Page 2: Gene Therapy Helps Hemophilia B Patients - ABC News

abcnews.go.com — “Gene therapy can overcome hemophila B, originally named Christmas disease.View full resource at abcnews.go.com

  • View Related
  • Share

Most Recently Shared on December 13, 2011 at 7:31 pm By:

Adults With Hemophilia B Benefit From Gene Therapy

medicalnewstoday.com — “Symptoms improved significantly in adults with the bleeding disorder hemophilia B following a single treatment with gene therapy developed by researchers at St. Jude Children's Research Hospital iView full resource at medicalnewstoday.com

  • View Related
  • Share

Most Recently Shared on December 13, 2011 at 8:05 am By:

Gene Therapy Helps Hemophilia B Patients - ABC News

abcnews.go.com — “Gene therapy can overcome hemophila B, originally named Christmas disease.View full resource at abcnews.go.com

  • View Related
  • Share

Most Recently Shared on December 12, 2011 at 3:48 pm By:

SusanS_Health Susan Scroggins Active Health Library and Health Advocate

Gene Therapy Offers Hope for Hemophilia B: Gene therapy can overcome hemophila B, originally named Christmas dis... http://t.co/LATqOiLf

6 months ago...

NYT: Hemophilia B Gene Therapy Brea

mobile.nytimes.com — “Hemophilia B is the first well-known disease to appear treatable by gene therapy, a technique with a 20-year record of almost unbroken failure.View full resource at mobile.nytimes.com

  • View Related
  • Share

Most Recently Shared on December 11, 2011 at 5:33 am By:

Atul_Gawande Atul Gawande Physician, Doctor, and Surgeon

Gene therapy actually succeeds, curing 6 Hemophilia B pts (at least temporarily). http://t.co/qMHBpgAS Cure far cheaper than chronic rx too.

6 months ago...

Gene therapy proves effective for hemophilia B | Reuters

reuters.com — “SAN DIEGO (Reuters) - A single treatment with gene therapy, an experimental technique for fixing faulty genes, has been shown to boost output of a vital blood clotting factor, possibly offering a long-termView full resource at reuters.com

  • View Related
  • Share

Most Recently Shared on December 11, 2011 at 3:21 am By:

Reuters_Health Reuters Health Health News

Gene therapy proves effective for hemophilia B http://t.co/3ByBGYXH

6 months ago...

Hemophilia B - Single Gene Therapy Treatment Offers Significant Improvement

medicalnewstoday.com — “Patients with hemophilia B experienced considerable improvements and fewer injections with clotting factor to reduce bleeding after receiving just one treatment with gene therapy, researchers fromView full resource at medicalnewstoday.com

  • View Related
  • Share

Most Recently Shared on December 10, 2011 at 8:05 pm By:

mnt_blood MNT Blood Health News

Hemophilia B - Single Gene Therapy Treatment Offers Significant Improvement http://t.co/1RVC3T8U #blood #hematology

6 months ago...

EMA grants orphan designation to AMT for hemophilia B gene therapy

news-medical.net — “Amsterdam Molecular Therapeutics, a leader in the field of human gene therapy, announced today that the European Medicines Agency (EMA) has granted orphan designation for its gene therapy program for the treatment of hemophilia B. Orphan designation in the European Union provides several benefits including 10 years of market exclusivity from product launch and access to the central authorization procedure.View full resource at news-medical.net

  • View Related
  • Share

Most Recently Shared on November 16, 2011 at 5:30 pm By:

Parkinsons_News News-Medical.Net Health News

Parkinson's Disease: EMA grants orphan designation to AMT for hemophilia B gene therapy: Amsterdam Molecular The... http://t.co/li0WP3Nm

6 months ago...

Genome editing improves blood clotting in mice with hemophilia B

medicalxpress.com — “(Medical Xpress) -- Scientists have used a gene therapy tool that acts like intelligent molecular scissors to correct the key gene defect in mice with hemophilia B, a disease that can lead to uncontrolled bleeding. The intervention improved the animals’ blood clotting enough that their severe disease ...View full resource at medicalxpress.com

  • View Related
  • Share

Most Recently Shared on June 28, 2011 at 4:46 pm By:

physorg_health PhysOrg Health News Health News

Genome editing improves blood clotting in mice with hemophilia B http://tw.medicalxpress.com/228483951

11 months ago...

Study Examines Novel Gene Therapy Approach For Severe Hemophilia B

medicalnewstoday.com — “A study examining novel gene therapy for the treatment of the bleeding disorder hemophilia B will be presented at the 52nd Annual Meeting of the American Society of Hematology. Hemophilia B is anView full resource at medicalnewstoday.com

  • View Related
  • Share

Most Recently Shared on December 8, 2010 at 5:05 pm By:

mnt_blood MNT Blood Health News

Study Examines Novel Gene Therapy Approach For Severe Hemophilia B http://mnt.to/3NJC #blood #hematology

1 year ago...

Early Safety Results Promising for Phase I/II Trial of Gene Therapy Treatment of Hemophilia B - Drugs.com MedNews

drugs.com — “Vector-gene combination developed at St. Jude Children s Research Hospital and UCL is central to latest clinical trial of gene therapy as a possible tool to proView full resource at drugs.com

  • View Related
  • Share

Most Recently Shared on December 7, 2010 at 9:07 pm By:

Drugs_Devices Drugs and Devices OW OW Health

Early Safety Results Promising for Phase I/II Trial of Gene Therapy Treatment of Hemophilia B: Vector-gene... http://bit.ly/gIu31v #drug

1 year ago...

Medical News: ASH: Early Gene Therapy Promising in Hemophilia - in Meeting Coverage, ASH: Hematology from MedPage Today

medpagetoday.com — “ORLANDO -- In early clinical trials, a single infusion of a novel viral vector containing a factor IX transgene has enabled one person with hemophilia B to increase clotting factors in his blood and mView full resource at medpagetoday.com

  • View Related
  • Share

Most Recently Shared on December 7, 2010 at 7:09 pm By:

MedicalNews Medical News Health News

ASH: Early Gene Therapy Promising in Hemophilia (CME/CE) http://bit.ly/hOsAse

1 year ago...

Early Safety Results Promising for Phase I/II Trial of Gene Therapy Treatment of Hemophilia B

newswise.com — “Investigators report no evidence of toxicity in the four hemophilia B patients enrolled to date in a gene therapy trial using a vector under development at St. Jude Children--™s Research Hospital and UCL (University College London) to correct the inherited bleeding disorder.View full resource at newswise.com

  • View Related
  • Share

Most Recently Shared on December 6, 2010 at 5:22 pm By:

newswise newswise Health Communicator and Health News

Early Safety Results Promising for Phase I/II Trial of Gene Therapy Treatment of Hemophilia B: Investigators rep... http://bit.ly/i9h1bw

1 year ago...

Advertisement