Gene therapy makes major stride in 'Lorenzo's Oil' disease - latimes.com

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Gene therapy makes major stride in 'Lorenzo's Oil' disease - latimes.com

In the third gene-therapy success of recent weeks, French researchers have arrested the progression of the rare and fatal degenerative disorder adrenoleukodystrophy, which was at the heart of the popular movie "Lorenzo's Oil." The disease has stabilized in two boys who were 7 years old when the therapy was performed two years ago, the team reported today in the journal Science.

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Tags: Heart, Disease and Condition, Genes